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Prader–Willi syndrome and early-onset morbid obesity NIH rare disease consortium: A review of natural history study

We describe the National Institutes of Health rare disease consortium for Prader-Willi syndrome (PWS) developed to address concerns regarding medical care, diagnosis, growth and development, awareness, and natural history. PWS results from errors in genomic imprinting leading to loss of paternally e...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Am J Med Genet A
Egile Nagusiak: Butler, Merlin G., Kimonis, Virginia, Dykens, Elisabeth, Gold, June A., Miller, Jennifer, Tamura, Roy, Driscoll, Daniel J.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2017
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC6065257/
https://ncbi.nlm.nih.gov/pubmed/29271568
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.a.38582
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