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New Medications in the Treatment of Hereditary Transthyretin Amyloidosis

Hereditary transthyretin amyloidosis is an inherited disorder that results in the gradual progressive deposit of abnormal protein called amyloid in the body’s organs and tissues. There are currently no approved drugs to treat transthyretin amyloidosis, and patients may require liver transplantation...

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Detalles Bibliográficos
Publicado en:Hosp Pharm
Autor principal: Walker, Scot
Formato: Artigo
Lenguaje:Inglês
Publicado: SAGE Publications 2018
Materias:
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC6050879/
https://ncbi.nlm.nih.gov/pubmed/30038442
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/0018578718779757
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