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Enhanced mRNA delivery into lymphocytes enabled by lipid-varied libraries of charge-altering releasable transporters

We report a strategy for generating a combinatorial library of oligonucleotide transporters with varied lipid domains and their use in the efficient transfection of lymphocytes with mRNA in vitro and in vivo. This library is based on amphiphilic charge-altering releasable transporters (CARTs) that c...

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Detalles Bibliográficos
Publicado en:Proc Natl Acad Sci U S A
Main Authors: McKinlay, Colin J., Benner, Nancy L., Haabeth, Ole A., Waymouth, Robert M., Wender, Paul A.
Formato: Artigo
Idioma:Inglês
Publicado: National Academy of Sciences 2018
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC6042134/
https://ncbi.nlm.nih.gov/pubmed/29891683
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.1805358115
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