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Utilizing ExAC to assess the hidden contribution of variants of unknown significance to Sanfilippo Type B incidence

Given the large and expanding quantity of publicly available sequencing data, it should be possible to extract incidence information for monogenic diseases from allele frequencies, provided one knows which mutations are causal. We tested this idea on a rare, monogenic, lysosomal storage disorder, Sa...

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Publicat a:PLoS One
Autors principals: Clark, Wyatt T., Yu, G. Karen, Aoyagi-Scharber, Mika, LeBowitz, Jonathan H.
Format: Artigo
Idioma:Inglês
Publicat: Public Library of Science 2018
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC6034809/
https://ncbi.nlm.nih.gov/pubmed/29979746
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0200008
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