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Mutant ataxin1 disrupts cerebellar development in spinocerebellar ataxia type 1

Spinocerebellar ataxia type 1 (SCA1) is an adult-onset neurodegenerative disease caused by a polyglutamine expansion in the protein ATXN1, which is involved in transcriptional regulation. Although symptoms appear relatively late in life, primarily from cerebellar dysfunction, pathogenesis begins ear...

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Detalles Bibliográficos
Publicado en:J Clin Invest
Main Authors: Edamakanti, Chandrakanth Reddy, Do, Jeehaeh, Didonna, Alessandro, Martina, Marco, Opal, Puneet
Formato: Artigo
Idioma:Inglês
Publicado: American Society for Clinical Investigation 2018
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC5983343/
https://ncbi.nlm.nih.gov/pubmed/29533923
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI96765
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