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The Horizon of a Therapy for Rare Genetic Diseases: A “Druggable” Future for Fibrodysplasia Ossificans Progressiva

Fibrodysplasia ossificans progressiva (FOP) is a rare genetic condition characterized by progressive extra-skeletal ossification leading to cumulative and severe disability. FOP has an extremely variable and episodic course and can be induced by trauma, infections, iatrogenic harms, immunization or...

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Foilsithe in:Int J Mol Sci
Main Authors: Cappato, Serena, Giacopelli, Francesca, Ravazzolo, Roberto, Bocciardi, Renata
Formáid: Artigo
Teanga:Inglês
Foilsithe: MDPI 2018
Ábhair:
Rochtain Ar Líne:https://ncbi.nlm.nih.gov/pmc/articles/PMC5979309/
https://ncbi.nlm.nih.gov/pubmed/29587443
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms19040989
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