Načítá se...

Small nuclear RNA-mediated modulation of splicing reveals a therapeutic strategy for a TREM2 mutation and its post-transcriptional regulation

Loss-of-function mutations in TREM2 cause Nasu-Hakola disease (NHD), a rare genetic disease characterized by early-onset dementia with leukoencephalopathy and bone cysts. An NHD-associated mutation, c.482 + 2 T > C, disrupts the splice donor site of intron 3 and causes aberrant skipping of exon 3...

Celý popis

Uloženo v:
Podrobná bibliografie
Vydáno v:Sci Rep
Hlavní autoři: Yanaizu, Motoaki, Sakai, Kenji, Tosaki, Youhei, Kino, Yoshihiro, Satoh, Jun-ichi
Médium: Artigo
Jazyk:Inglês
Vydáno: Nature Publishing Group UK 2018
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5931963/
https://ncbi.nlm.nih.gov/pubmed/29720600
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41598-018-25204-2
Tagy: Přidat tag
Žádné tagy, Buďte první, kdo otaguje tento záznam!