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CRISPR/Cas9 Technology as an Emerging Tool for Targeting Amyotrophic Lateral Sclerosis (ALS)

The clustered regularly interspaced short palindromic repeats (CRISPR)/CRISPR-associated protein-9 nuclease (Cas9) is a genome editing tool that has recently caught enormous attention due to its novelty, feasibility, and affordability. This system naturally functions as a defense mechanism in bacter...

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Detalhes bibliográficos
Publicado no:Int J Mol Sci
Main Authors: Kruminis-Kaszkiel, Ewa, Juranek, Judyta, Maksymowicz, Wojciech, Wojtkiewicz, Joanna
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2018
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5877767/
https://ncbi.nlm.nih.gov/pubmed/29562705
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms19030906
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