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Chromothripsis and ring chromosome 22: a paradigm of genomic complexity in the Phelan-McDermid syndrome (22q13 deletion syndrome)

INTRODUCTION: Phelan-McDermid syndrome (PMS) is caused by SHANK3 haploinsufficiency. Its wide phenotypic variation is attributed partly to the type and size of 22q13 genomic lesion (deletion, unbalanced translocation, ring chromosome), partly to additional undefined factors. We investigated a child...

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Bibliografski detalji
Izdano u:J Med Genet
Glavni autori: Kurtas, Nehir, Arrigoni, Filippo, Errichiello, Edoardo, Zucca, Claudio, Maghini, Cristina, D’Angelo, Maria Grazia, Beri, Silvana, Giorda, Roberto, Bertuzzo, Sara, Delledonne, Massimo, Xumerle, Luciano, Rossato, Marzia, Zuffardi, Orsetta, Bonaglia, Maria Clara
Format: Artigo
Jezik:Inglês
Izdano: BMJ Publishing Group 2018
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5869459/
https://ncbi.nlm.nih.gov/pubmed/29378768
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1136/jmedgenet-2017-105125
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