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Dual AAV Gene Therapy for Duchenne Muscular Dystrophy with a 7-kb Mini-Dystrophin Gene in the Canine Model

Dual adeno-associated virus (AAV) technology was developed in 2000 to double the packaging capacity of the AAV vector. The proof of principle has been demonstrated in various mouse models. Yet, pivotal evidence is lacking in large animal models of human diseases. Here we report expression of a 7-kb...

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Dettagli Bibliografici
Pubblicato in:Hum Gene Ther
Autori principali: Kodippili, Kasun, Hakim, Chady H., Pan, Xiufang, Yang, Hsiao T., Yue, Yongping, Zhang, Yadong, Shin, Jin-Hong, Yang, N. Nora, Duan, Dongsheng
Natura: Artigo
Lingua:Inglês
Pubblicazione: Mary Ann Liebert, Inc. 2018
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5865264/
https://ncbi.nlm.nih.gov/pubmed/28793798
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2017.095
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