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Treatment with Creatine Monohydrate in Spinal and Bulbar Muscular Atrophy: Protocol for a Randomized, Double-Blind, Placebo-Controlled Trial

BACKGROUND: Although spinal and bulbar muscular atrophy (SBMA) has been classified as a motor neuron disease, several reports have indicated the primary involvement of skeletal muscle in the pathogenesis of this devastating disease. Recent studies reported decreased intramuscular creatine levels in...

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Dades bibliogràfiques
Publicat a:JMIR Res Protoc
Autors principals: Hijikata, Yasuhiro, Katsuno, Masahisa, Suzuki, Keisuke, Hashizume, Atsushi, Araki, Amane, Yamada, Shinichiro, Inagaki, Tomonori, Ito, Daisuke, Hirakawa, Akihiro, Kinoshita, Fumie, Gosho, Masahiko, Sobue, Gen
Format: Artigo
Idioma:Inglês
Publicat: JMIR Publications 2018
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5859194/
https://ncbi.nlm.nih.gov/pubmed/29506970
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2196/resprot.8655
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