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Diverse Phenotypic Expression of NPHP4 Mutations in Four Siblings

Nephronophthisis (NPHP) is an autosomal recessive disease characterized by renal tubular basement membrane disruption, interstitial fibrosis, and tubular cysts that progresses to end-stage kidney disease (ESKD). There are characteristic extrarenal manifestations. Mutations of more than thirteen gene...

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Detalles Bibliográficos
Publicado en:Turk J Pediatr
Main Authors: Bakkaloğlu, Sevcan A., Kandur, Yaşar, Demirdağ, Tuğba Bedir, Gönül, İpek Işık, Hildebrandt, Friedhelm
Formato: Artigo
Idioma:Inglês
Publicado: 2014
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC5839637/
https://ncbi.nlm.nih.gov/pubmed/25818963
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