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Functional improvements in patients with lymphangioleiomyomatosis after sirolimus: an observational study

BACKGROUND: Sirolimus has been shown to be effective in patients with lymphangioleiomyomatosis (LAM). We wish to summarize our experience using sirolimus and its effectiveness in LAM patients. METHODS: We analyzed data from 98 patients who were diagnosed with definite or probable sporadic LAM based...

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Detalhes bibliográficos
Publicado no:Orphanet J Rare Dis
Main Authors: Zhan, Yongzhong, Shen, Lisha, Xu, Wenshuai, Wu, Xiuxiu, Zhang, Weihong, Wang, Jun, Li, Xue, Yang, Yanli, Tian, Xinlun, Xu, Kai-Feng
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2018
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5819088/
https://ncbi.nlm.nih.gov/pubmed/29458386
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-018-0775-9
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