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Correlation between urinary GAG and anti-idursulfase ERT neutralizing antibodies during treatment with NICIT immune tolerance regimen: A case report(,)

INTRODUCTION: Antibodies to intravenous idursulfase enzyme replacement therapy (ERT) for patients with Hunter syndrome (mucopolysaccharidosis type II, MPS II) can have a harmful clinical impact, including both increasing risk of infusion reactions and inhibiting therapeutic activity. Thus, failure t...

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Publicat a:Mol Genet Metab
Autors principals: Kim, Sarah, Whitley, Chester B., Jarnes Utz, Jeanine R.
Format: Artigo
Idioma:Inglês
Publicat: 2017
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5798249/
https://ncbi.nlm.nih.gov/pubmed/28610913
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymgme.2017.06.001
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