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Guanidinoacetate Methyltransferase Activity in Lymphocytes, for a Fast Diagnosis

Introduction. Guanidinoacetate methyltransferase (GAMT) deficiency is an inborn error of metabolism (IEM), clinically characterized by intellectual disability, developmental delay, seizures, and movement disorders. Biochemical diagnosis of GAMT deficiency is based on the measurement of creatine and...

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Dettagli Bibliografici
Pubblicato in:JIMD Rep
Autori principali: Berends, Lisette M., Struys, Eduard A., Roos, Birthe, Holwerda, Ulbe, Jansen, Erwin E. W., Salomons, Gajja S., Wamelink, Mirjam M. C.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer Berlin Heidelberg 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5740046/
https://ncbi.nlm.nih.gov/pubmed/28220408
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2017_4
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