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Medium chain acyl-CoA dehydrogenase deficiency in a premature infant

Medium-chain acyl-CoA dehydrogenase deficiency (MCADD) is identified by newborn screening (NBS). The natural history of MCADD includes metabolic decompensation with hypoglycemia, hyperammonemia, seizures, coma, and death. NBS enables expectant management thus severe symptoms are rare in managed pati...

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Detalhes bibliográficos
Publicado no:Pediatr Rep
Main Authors: Dobrowolski, Steven F., Ghaloul-Gonzalez, Lina, Vockley, Jerry
Formato: Artigo
Idioma:Inglês
Publicado em: PAGEPress Scientific Publications, Pavia, Italy 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5733391/
https://ncbi.nlm.nih.gov/pubmed/29285339
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4081/pr.2017.7045
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