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Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia
Beta-thalassemia and sickle cell anemia are two of the most common diseases related to the hemoglobin protein. In these diseases, the beta-globin gene is mutated, causing severe anemia and ineffective erythropoiesis. Patients can additionally present with a number of life-threatening co-morbidities,...
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| Publicado en: | Adv Exp Med Biol |
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| Autores principales: | , |
| Formato: | Artigo |
| Lenguaje: | Inglês |
| Publicado: |
2017
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| Materias: | |
| Acceso en línea: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5718882/ https://ncbi.nlm.nih.gov/pubmed/29127680 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/978-1-4939-7299-9_6 |
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