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Spinal Muscular Atrophy: The Treatment Approved

Spinal muscular atrophy (SMA) is a rare genetic neuromuscular disorder resulting in progressive muscle weakness and atrophy. It is universally fatal, especially if the respiratory muscles are involved leading to repetitive aspiration and respiratory failure. Historically, the treatment for this dise...

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Detalles Bibliográficos
Publicado en:Cureus
Main Authors: Tabet, Rabih, El Bitar, Sandy, Zaidan, Julie, Dabaghian, Garbis
Formato: Artigo
Idioma:Inglês
Publicado: Cureus 2017
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC5669527/
https://ncbi.nlm.nih.gov/pubmed/29142792
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.7759/cureus.1644
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