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Spinal Muscular Atrophy: The Treatment Approved
Spinal muscular atrophy (SMA) is a rare genetic neuromuscular disorder resulting in progressive muscle weakness and atrophy. It is universally fatal, especially if the respiratory muscles are involved leading to repetitive aspiration and respiratory failure. Historically, the treatment for this dise...
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| Pubblicato in: | Cureus |
|---|---|
| Autori principali: | , , , |
| Natura: | Artigo |
| Lingua: | Inglês |
| Pubblicazione: |
Cureus
2017
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| Soggetti: | |
| Accesso online: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5669527/ https://ncbi.nlm.nih.gov/pubmed/29142792 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.7759/cureus.1644 |
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