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Silencing Nfix rescues muscular dystrophy by delaying muscle regeneration

Muscular dystrophies are severe disorders due to mutations in structural genes, and are characterized by skeletal muscle wasting, compromised patient mobility, and respiratory functions. Although previous works suggested enhancing regeneration and muscle mass as therapeutic strategies, these led to...

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Dettagli Bibliografici
Pubblicato in:Nat Commun
Autori principali: Rossi, Giuliana, Bonfanti, Chiara, Antonini, Stefania, Bastoni, Mattia, Monteverde, Stefania, Innocenzi, Anna, Saclier, Marielle, Taglietti, Valentina, Messina, Graziella
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group UK 2017
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5651883/
https://ncbi.nlm.nih.gov/pubmed/29057908
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41467-017-01098-y
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