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Silencing Nfix rescues muscular dystrophy by delaying muscle regeneration

Muscular dystrophies are severe disorders due to mutations in structural genes, and are characterized by skeletal muscle wasting, compromised patient mobility, and respiratory functions. Although previous works suggested enhancing regeneration and muscle mass as therapeutic strategies, these led to...

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Bibliografiske detaljer
Udgivet i:Nat Commun
Main Authors: Rossi, Giuliana, Bonfanti, Chiara, Antonini, Stefania, Bastoni, Mattia, Monteverde, Stefania, Innocenzi, Anna, Saclier, Marielle, Taglietti, Valentina, Messina, Graziella
Format: Artigo
Sprog:Inglês
Udgivet: Nature Publishing Group UK 2017
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC5651883/
https://ncbi.nlm.nih.gov/pubmed/29057908
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41467-017-01098-y
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