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Developing a Natural History Progression Model for Duchenne Muscular Dystrophy Using the Six‐Minute Walk Test

The 6‐minute walk test (6MWT) is used as a clinical endpoint to evaluate drug efficacy in Duchenne Muscular Dystrophy (DMD) trials. A model was developed using digitized 6MWT data that estimated two slopes and two intercepts to characterize 6MWT improvement during development and 6MWT decline. Mean...

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Detalhes bibliográficos
Publicado no:CPT Pharmacometrics Syst Pharmacol
Main Authors: Hamuro, Lora, Chan, Phyllis, Tirucherai, Giridhar, AbuTarif, Malaz
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley and Sons Inc. 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5613187/
https://ncbi.nlm.nih.gov/pubmed/28643370
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/psp4.12220
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