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Categorizing natural history trajectories of ambulatory function measured by the 6-minute walk distance in patients with Duchenne muscular dystrophy

High variability in patients' changes in 6 minute walk distance (6MWD) over time has complicated clinical trials of treatment efficacy in Duchenne muscular dystrophy (DMD). We assessed whether boys with DMD could be grouped into classes that shared similar ambulatory function trajectories as me...

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Bibliografiske detaljer
Udgivet i:Neuromuscul Disord
Main Authors: Mercuri, Eugenio, Signorovitch, James Edward, Swallow, Elyse, Song, Jinlin, Ward, Susan J.
Format: Artigo
Sprog:Inglês
Udgivet: Pergamon Press 2016
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC5026045/
https://ncbi.nlm.nih.gov/pubmed/27423700
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.nmd.2016.05.016
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