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A functional scale for spinal and bulbar muscular atrophy: Cross-sectional and longitudinal study

We aimed to develop, validate, and evaluate a disease-specific outcome measure for SBMA: the Spinal and Bulbar Muscular Atrophy Functional Rating Scale (SBMAFRS). We examined the Japanese version (SBMAFRS-J) in 80 Japanese SBMA subjects to evaluate its validity and reliability. We then assessed this...

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Bibliografiske detaljer
Udgivet i:Neuromuscul Disord
Main Authors: Hashizume, Atsushi, Katsuno, Masahisa, Suzuki, Keisuke, Banno, Haruhiko, Suga, Noriaki, Mano, Tomoo, Araki, Amane, Hijikata, Yasuhiro, Grunseich, Christopher, Kokkinis, Angela, Hirakawa, Akihiro, Watanabe, Hirohisa, Yamamoto, Masahiko, Fischbeck, Kenneth H., Sobue, Gen
Format: Artigo
Sprog:Inglês
Udgivet: 2015
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC5608513/
https://ncbi.nlm.nih.gov/pubmed/25913211
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.nmd.2015.03.008
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