Using CRISPR-Cas9 to Generate Gene-Corrected Autologous iPSCs for the Treatment of Inherited Retinal Degeneration

Patient-derived induced pluripotent stem cells (iPSCs) hold great promise for autologous cell replacement. However, for many inherited diseases, treatment will likely require genetic repair pre-transplantation. Genome editing technologies are useful for this application. The purpose of this study wa...

全面介紹

Na minha lista:
書目詳細資料
發表在:Mol Ther
Main Authors: Burnight, Erin R., Gupta, Manav, Wiley, Luke A., Anfinson, Kristin R., Tran, Audrey, Triboulet, Robinson, Hoffmann, Jeremy M., Klaahsen, Darcey L., Andorf, Jeaneen L., Jiao, Chunhua, Sohn, Elliott H., Adur, Malavika K., Ross, Jason W., Mullins, Robert F., Daley, George Q., Schlaeger, Thorsten M., Stone, Edwin M., Tucker, Budd A.
格式: Artigo
語言:Inglês
出版: American Society of Gene & Cell Therapy 2017
主題:
Original Article
在線閱讀:https://ncbi.nlm.nih.gov/pmc/articles/PMC5589061/
https://ncbi.nlm.nih.gov/pubmed/28619647
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2017.05.015
標簽: 添加標簽
沒有標簽, 成為第一個標記此記錄!

相似書籍