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Cerebrotendinous Xanthomatosis Presenting with Infantile Spasms and Intellectual Disability

Cerebrotendinous xanthomatosis (CTX) is an inborn error of metabolism leading to progressive multisystem disease. Symptoms often begin in the first decade of life with chronic diarrhea, cataracts, developmental delay, intellectual disability, and cerebellar or pyramidal dysfunction. Later manifestat...

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Publicat a:JIMD Rep
Autors principals: Larson, Austin, Weisfeld-Adams, James D., Benke, Tim A., Bonnen, Penelope E.
Format: Artigo
Idioma:Inglês
Publicat: Springer Berlin Heidelberg 2016
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5585103/
https://ncbi.nlm.nih.gov/pubmed/27858369
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2016_16
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