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Cerebrotendinous Xanthomatosis Presenting with Infantile Spasms and Intellectual Disability

Cerebrotendinous xanthomatosis (CTX) is an inborn error of metabolism leading to progressive multisystem disease. Symptoms often begin in the first decade of life with chronic diarrhea, cataracts, developmental delay, intellectual disability, and cerebellar or pyramidal dysfunction. Later manifestat...

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Dettagli Bibliografici
Pubblicato in:JIMD Rep
Autori principali: Larson, Austin, Weisfeld-Adams, James D., Benke, Tim A., Bonnen, Penelope E.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer Berlin Heidelberg 2016
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5585103/
https://ncbi.nlm.nih.gov/pubmed/27858369
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2016_16
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