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In Vivo Base Editing of PCSK9 as a Therapeutic Alternative to Genome Editing

OBJECTIVE: High-efficiency genome editing to disrupt therapeutic target genes such as PCSK9 has been demonstrated in preclinical animal models, but there are safety concerns due to the unpredictable nature of cellular repair of double-strand breaks, as well as off-target mutagenesis. Moreover, preci...

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Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Arterioscler Thromb Vasc Biol
Egile Nagusiak: Chadwick, Alexandra C., Wang, Xiao, Musunuru, Kiran
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: 2017
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5570639/
https://ncbi.nlm.nih.gov/pubmed/28751571
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1161/ATVBAHA.117.309881
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