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In Vivo Base Editing of PCSK9 as a Therapeutic Alternative to Genome Editing

OBJECTIVE: High-efficiency genome editing to disrupt therapeutic target genes such as PCSK9 has been demonstrated in preclinical animal models, but there are safety concerns due to the unpredictable nature of cellular repair of double-strand breaks, as well as off-target mutagenesis. Moreover, preci...

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Библиографические подробности
Опубликовано в: :Arterioscler Thromb Vasc Biol
Главные авторы: Chadwick, Alexandra C., Wang, Xiao, Musunuru, Kiran
Формат: Artigo
Язык:Inglês
Опубликовано: 2017
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC5570639/
https://ncbi.nlm.nih.gov/pubmed/28751571
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1161/ATVBAHA.117.309881
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