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Mesenchymal Stem Cell-Derived Factors Restore Function to Human Frataxin-Deficient Cells

Friedreich’s ataxia is an inherited neurological disorder characterised by mitochondrial dysfunction and increased susceptibility to oxidative stress. At present, no therapy has been shown to reduce disease progression. Strategies being trialled to treat Friedreich’s ataxia include drugs that improv...

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Publicat a:Cerebellum
Autors principals: Kemp, Kevin, Dey, Rimi, Cook, Amelia, Scolding, Neil, Wilkins, Alastair
Format: Artigo
Idioma:Inglês
Publicat: Springer US 2017
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5498643/
https://ncbi.nlm.nih.gov/pubmed/28456899
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s12311-017-0860-y
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