Načítá se...

The role of sebelipase alfa in the treatment of lysosomal acid lipase deficiency

Lysosomal acid lipase deficiency (LALD) is a lysosomal storage disorder (LSD) characterized either by infantile onset with fulminant clinical course and very poor prognosis or childhood/adult-onset disease with an attenuated phenotype. The disorder is often misdiagnosed or remains undiagnosed in chi...

Celý popis

Uloženo v:
Podrobná bibliografie
Vydáno v:Therap Adv Gastroenterol
Hlavní autor: Erwin, Angelika L.
Médium: Artigo
Jazyk:Inglês
Vydáno: SAGE Publications 2017
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5484437/
https://ncbi.nlm.nih.gov/pubmed/28804516
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1177/1756283X17705775
Tagy: Přidat tag
Žádné tagy, Buďte první, kdo otaguje tento záznam!