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Primary Ciliary Dyskinesia: An Update on Clinical Aspects, Genetics, Diagnosis, and Future Treatment Strategies

Primary ciliary dyskinesia (PCD) is an orphan disease (MIM 244400), autosomal recessive inherited, characterized by motile ciliary dysfunction. The estimated prevalence of PCD is 1:10,000 to 1:20,000 live-born children, but true prevalence could be even higher. PCD is characterized by chronic upper...

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Detalles Bibliográficos
Publicado en:Front Pediatr
Main Authors: Mirra, Virginia, Werner, Claudius, Santamaria, Francesca
Formato: Artigo
Idioma:Inglês
Publicado: Frontiers Media S.A. 2017
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC5465251/
https://ncbi.nlm.nih.gov/pubmed/28649564
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fped.2017.00135
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