Myogenic differentiation of VCP disease-induced pluripotent stem cells: A novel platform for drug discovery

Valosin Containing Protein (VCP) disease is an autosomal dominant multisystem proteinopathy caused by mutations in the VCP gene, and is primarily associated with progressive muscle weakness, including atrophy of the pelvic and shoulder girdle muscles. Currently, no treatments are available and cardi...

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Bibliographic Details
Published in:PLoS One
Main Authors: Llewellyn, Katrina J., Nalbandian, Angèle, Weiss, Lan N., Chang, Isabela, Yu, Howard, Khatib, Bibo, Tan, Baichang, Scarfone, Vanessa, Kimonis, Virginia E.
Format: Artigo
Language:Inglês
Published: Public Library of Science 2017
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Research Article
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC5456028/
https://ncbi.nlm.nih.gov/pubmed/28575052
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0176919
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