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A risk factor analysis of outcomes after unrelated cord blood transplantation for children with Wiskott-Aldrich syndrome

Wiskott-Aldrich syndrome is a severe X-linked recessive immune deficiency disorder. A scoring system of Wiskott-Aldrich syndrome severity (0.5–5) distinguishes two phenotypes: X-linked thrombocytopenia and classic Wiskott-Aldrich syndrome. Hematopoietic cell transplantation is curative for Wiskott-A...

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Detaylı Bibliyografya
Yayımlandı:Haematologica
Asıl Yazarlar: Shekhovtsova, Zhanna, Bonfim, Carmem, Ruggeri, Annalisa, Nichele, Samantha, Page, Kristin, AlSeraihy, Amal, Barriga, Francisco, de Toledo Codina, José Sánchez, Veys, Paul, Boelens, Jaap Jan, Mellgren, Karin, Bittencourt, Henrique, O’Brien, Tracey, Shaw, Peter J., Chybicka, Alicja, Volt, Fernanda, Giannotti, Federica, Gluckman, Eliane, Kurtzberg, Joanne, Gennery, Andrew R., Rocha, Vanderson
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Ferrata Storti Foundation 2017
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5451344/
https://ncbi.nlm.nih.gov/pubmed/28255019
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2016.158808
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