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A risk factor analysis of outcomes after unrelated cord blood transplantation for children with Wiskott-Aldrich syndrome

Wiskott-Aldrich syndrome is a severe X-linked recessive immune deficiency disorder. A scoring system of Wiskott-Aldrich syndrome severity (0.5–5) distinguishes two phenotypes: X-linked thrombocytopenia and classic Wiskott-Aldrich syndrome. Hematopoietic cell transplantation is curative for Wiskott-A...

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Detalhes bibliográficos
Publicado no:Haematologica
Main Authors: Shekhovtsova, Zhanna, Bonfim, Carmem, Ruggeri, Annalisa, Nichele, Samantha, Page, Kristin, AlSeraihy, Amal, Barriga, Francisco, de Toledo Codina, José Sánchez, Veys, Paul, Boelens, Jaap Jan, Mellgren, Karin, Bittencourt, Henrique, O’Brien, Tracey, Shaw, Peter J., Chybicka, Alicja, Volt, Fernanda, Giannotti, Federica, Gluckman, Eliane, Kurtzberg, Joanne, Gennery, Andrew R., Rocha, Vanderson
Formato: Artigo
Idioma:Inglês
Publicado em: Ferrata Storti Foundation 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5451344/
https://ncbi.nlm.nih.gov/pubmed/28255019
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2016.158808
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