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Modern Genome Editing Technologies in Huntington’s Disease Research

The development of new revolutionary technologies for directed gene editing has made it possible to thoroughly model and study NgAgo human diseases at the cellular and molecular levels. Gene editing tools like ZFN, TALEN, CRISPR-based systems, NgAgo and SGN can introduce different modifications. In...

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Dades bibliogràfiques
Publicat a:J Huntingtons Dis
Autors principals: Malankhanova, Tuyana B., Malakhova, Anastasia A., Medvedev, Sergey P., Zakian, Suren M.
Format: Artigo
Idioma:Inglês
Publicat: IOS Press 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5389024/
https://ncbi.nlm.nih.gov/pubmed/28128770
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3233/JHD-160222
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