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A de novo splice site mutation in EHMT1 resulting in Kleefstra syndrome with pharmacogenomics screening and behavior therapy for regressive behaviors

BACKGROUND: Kleefstra syndrome (KS) is a rare autosomal dominant developmental disability, caused by microdeletions or intragenic mutations within the epigenetic regulator gene EHMT1 (euchromatic histone lysine N‐methyltransferase 1). In addition to common features of autism, young adult regressive...

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Dades bibliogràfiques
Publicat a:Mol Genet Genomic Med
Autors principals: Mitra, Amit Kumar, Dodge, Jessica, Van Ness, Jody, Sokeye, Israel, Van Ness, Brian
Format: Artigo
Idioma:Inglês
Publicat: John Wiley and Sons Inc. 2016
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5370220/
https://ncbi.nlm.nih.gov/pubmed/28361099
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/mgg3.265
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