Therapeutic response to intravenous infusions of glucocerebrosidase in a patient with Gaucher disease.
Enzyme replacement has been under consideration as a therapeutic strategy for patients with Gaucher disease for more than two decades. Previous studies indicated that single injections of purified glucocerebrosidase reduced the amount of storage material in the liver. It was important to determine w...
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| Publié dans: | Proc Natl Acad Sci U S A |
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| Auteurs principaux: | , , , , |
| Format: | Artigo |
| Langue: | Inglês |
| Publié: |
National Academy of Sciences
1990
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| Sujets: | |
| Accès en ligne: | https://ncbi.nlm.nih.govhttps://pmc.ncbi.nlm.nih.gov/articles/PMC53594/ https://ncbi.nlm.nih.govhttps://pubmed.ncbi.nlm.nih.gov/2308952/ https://ncbi.nlm.nih.govhttps://doi.org/10.1073/pnas.87.5.1913 |
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