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Familial amyloid polyneuropathy in Portugal: New genes modulating age‐at‐onset

OBJECTIVES: Familial amyloid polyneuropathy (FAP ATTRV30M) shows a wide variation in age‐at‐onset (AO) between clusters, families, and among generations. We will now explore some candidate genes involved in altered disease pathways in order to assess their role as genetic modifiers of AO, using a fa...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Ann Clin Transl Neurol
Egile Nagusiak: Santos, Diana, Coelho, Teresa, Alves‐Ferreira, Miguel, Sequeiros, Jorge, Mendonça, Denisa, Alonso, Isabel, Lemos, Carolina, Sousa, Alda
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: John Wiley and Sons Inc. 2016
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC5288465/
https://ncbi.nlm.nih.gov/pubmed/28168209
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/acn3.380
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