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mRNA trans‐splicing in gene therapy for genetic diseases

Spliceosome‐mediated RNA trans‐splicing, or SMaRT, is a promising strategy to design innovative gene therapy solutions for currently intractable genetic diseases. SMaRT relies on the correction of mutations at the post‐transcriptional level by modifying the mRNA sequence. To achieve this, an exogeno...

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Dettagli Bibliografici
Pubblicato in:Wiley Interdiscip Rev RNA
Autori principali: Berger, Adeline, Maire, Séverine, Gaillard, Marie‐Claude, Sahel, José‐Alain, Hantraye, Philippe, Bemelmans, Alexis‐Pierre
Natura: Artigo
Lingua:Inglês
Pubblicazione: John Wiley & Sons, Inc. 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5071737/
https://ncbi.nlm.nih.gov/pubmed/27018401
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/wrna.1347
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