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mRNA trans‐splicing in gene therapy for genetic diseases

Spliceosome‐mediated RNA trans‐splicing, or SMaRT, is a promising strategy to design innovative gene therapy solutions for currently intractable genetic diseases. SMaRT relies on the correction of mutations at the post‐transcriptional level by modifying the mRNA sequence. To achieve this, an exogeno...

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Detalhes bibliográficos
Publicado no:Wiley Interdiscip Rev RNA
Main Authors: Berger, Adeline, Maire, Séverine, Gaillard, Marie‐Claude, Sahel, José‐Alain, Hantraye, Philippe, Bemelmans, Alexis‐Pierre
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley & Sons, Inc. 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5071737/
https://ncbi.nlm.nih.gov/pubmed/27018401
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/wrna.1347
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