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Mutant PFN1 causes ALS phenotypes and progressive motor neuron degeneration in mice by a gain of toxicity

Mutations in the profilin 1 (PFN1) gene cause amyotrophic lateral sclerosis (ALS), a neurodegenerative disease caused by the loss of motor neurons leading to paralysis and eventually death. PFN1 is a small actin-binding protein that promotes formin-based actin polymerization and regulates numerous c...

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Dades bibliogràfiques
Publicat a:Proc Natl Acad Sci U S A
Autors principals: Yang, Chunxing, Danielson, Eric W., Qiao, Tao, Metterville, Jake, Brown, Robert H., Landers, John E., Xu, Zuoshang
Format: Artigo
Idioma:Inglês
Publicat: National Academy of Sciences 2016
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5068285/
https://ncbi.nlm.nih.gov/pubmed/27681617
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.1605964113
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