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An Expert Review of Pharmacogenomics of Sickle Cell Disease Therapeutics: Not Yet Ready for Global Precision Medicine

Sickle cell disease (SCD) is a blood disease caused by a single nucleotide substitution (T > A) in the beta globin gene on chromosome 11. The single point mutation (Glu6Val) promotes polymerization of hemoglobin S (HbS) and causes sickling of erythrocytes. Vaso-occlusive painful crises are associ...

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Publicat a:OMICS
Autors principals: Mnika, Khuthala, Pule, Gift D., Dandara, Collet, Wonkam, Ambroise
Format: Artigo
Idioma:Inglês
Publicat: Mary Ann Liebert, Inc. 2016
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5067801/
https://ncbi.nlm.nih.gov/pubmed/27636225
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/omi.2016.0105
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