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GM2-Gangliosidosis, AB Variant: Clinical, Ophthalmological, MRI, and Molecular Findings

GM2-gangliosidosis, AB variant is a very rare form of GM2 gangliosidosis due to a deficiency of GM2 activator protein, associated with autosomal recessive mutations in GM2A. Less than ten patients, confirmed by molecular analysis, have been described in the literature. A 12-month-old Hmong girl pres...

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Bibliografski detalji
Izdano u:JIMD Rep
Glavni autori: Renaud, Deborah, Brodsky, Michael
Format: Artigo
Jezik:Inglês
Izdano: Springer Berlin Heidelberg 2015
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC5059184/
https://ncbi.nlm.nih.gov/pubmed/26082327
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2015_469
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