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Everolimus safety and efficacy for renal angiomyolipomas associated with tuberous sclerosis complex: a Spanish expanded access trial

BACKGROUND: Renal angiomyolipomas (AML) are usual manifestations of tuberous sclerosis complex (TSC) that may cause aneurism-related haemorrhages and renal impairment. Everolimus has emerged as an alternative to surgery/embolization. We provide further insight into everolimus safety and efficacy for...

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Detaylı Bibliyografya
Yayımlandı:Orphanet J Rare Dis
Asıl Yazarlar: Robles, Nicolás Roberto, Peces, Ramón, Gómez-Ferrer, Álvaro, Villacampa, Felipe, Álvarez-Ossorio, Jose Luis, Pérez-Segura, Pedro, Morote, Juan, Herrera-Imbroda, Bernardo, Nieto, Javier, Carballido, Joaquín, Anido, Urbano, Valero, Marian, Meseguer, Cristina, Torra, Roser
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: BioMed Central 2016
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC5037621/
https://ncbi.nlm.nih.gov/pubmed/27669821
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-016-0517-9
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