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New therapeutic approaches for Krabbe disease: The potential of pharmacological chaperones

Missense mutations in the lysosomal hydrolase β‐galactocerebrosidase (GALC) account for at least 40% of known cases of Krabbe disease (KD). Most of these missense mutations are predicted to disrupt the fold of the enzyme, preventing GALC in sufficient amounts from reaching its site of action in the...

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Detalhes bibliográficos
Publicado no:J Neurosci Res
Main Authors: Spratley, Samantha J., Deane, Janet E.
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley and Sons Inc. 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC5031207/
https://ncbi.nlm.nih.gov/pubmed/27638604
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jnr.23762
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