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Quantum dots and potential therapy of Krabbe disease

Enzyme replacement therapy and substrate reduction therapy have proved useful in reversing many pathological consequences of many non-neural lysosomal storage diseases but have not yet reversed pathology or influenced disease outcome in Krabbe disease, We will discuss the relative merits of stem cel...

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Pubblicato in:J Neurosci Res
Autore principale: Dawson, Glyn
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2016
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC5027984/
https://ncbi.nlm.nih.gov/pubmed/27638611
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jnr.23805
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