Durable and sustained immune tolerance to ERT in Pompe disease with entrenched immune responses

BACKGROUND. Enzyme replacement therapy (ERT) has prolonged survival and improved clinical outcomes in patients with infantile Pompe disease (IPD), a rapidly progressive neuromuscular disorder. Yet marked interindividual variability in response to ERT, primarily attributable to the development of ant...

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Detaylı Bibliyografya
Yayımlandı:JCI Insight
Asıl Yazarlar: Kazi, Zoheb B., Prater, Sean N., Kobori, Joyce A., Viskochil, David, Bailey, Carrie, Gera, Renuka, Stockton, David W., McIntosh, Paul, Rosenberg, Amy S., Kishnani, Priya S.
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: American Society for Clinical Investigation 2016
Konular:
Clinical Medicine
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC4970756/
https://ncbi.nlm.nih.gov/pubmed/27493997
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/jci.insight.86821
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