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Treosulfan-based conditioning for allogeneic HSCT in children with chronic granulomatous disease: a multicenter experience

Chronic granulomatous disease (CGD) can be cured by allogeneic hemopoietic stem cell transplantation (HSCT). Complications include graft failure, graft-versus-host disease (GVHD), infection, and transplant-related mortality; therefore, reduced-intensity conditioning regimens are being used to improv...

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Detalhes bibliográficos
Publicado no:Blood
Main Authors: Morillo-Gutierrez, Beatriz, Beier, Rita, Rao, Kanchan, Burroughs, Lauri, Schulz, Ansgar, Ewins, Anna-Maria, Gibson, Brenda, Sedlacek, Petr, Krol, Ladislav, Strahm, Brigitte, Zaidman, Irina, Kalwak, Krzysztof, Talano, Julie-An, Woolfrey, Ann, Fraser, Chris, Meyts, Isabelle, Müller, Ingo, Wachowiak, Jacek, Bernardo, Maria Ester, Veys, Paul, Sykora, Karl-Walter, Gennery, Andrew R., Slatter, Mary
Formato: Artigo
Idioma:Inglês
Publicado em: American Society of Hematology 2016
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4957165/
https://ncbi.nlm.nih.gov/pubmed/27216217
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2016-03-704015
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