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Engineering Periodic shRNA for Enhanced Silencing Efficacy
RNA interference (RNAi) provides a versatile therapeutic approach via silencing of specific genes, particularly undruggable targets in cancer and other diseases. However, challenges in the delivery of small interfering RNA (siRNA) have hampered clinical translation. Polymeric or periodic short hairp...
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| Pubblicato in: | Mol Ther |
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| Autori principali: | , , |
| Natura: | Artigo |
| Lingua: | Inglês |
| Pubblicazione: |
Nature Publishing Group
2016
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| Soggetti: | |
| Accesso online: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4923333/ https://ncbi.nlm.nih.gov/pubmed/27053374 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2016.69 |
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