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Severe short stature in two siblings as the presenting sign of ACP5 deficiency

BACKGROUND: ACP5 deficiency is known to cause spondyloenchondrodysplasia (SPENCD), which is characterized by various auto-immune and neurological symptoms in addition to short stature. METHODS: Two siblings from a consanguineous Turkish family, a girl age 13 (P1) and a boy age 8 (P2), presented to t...

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Publicado en:Horm Res Paediatr
Main Authors: de Bruin, Christiaan, Orbak, Zerrin, Andrew, Melissa, Hwa, Vivian, Dauber, Andrew
Formato: Artigo
Idioma:Inglês
Publicado: 2016
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC4891295/
https://ncbi.nlm.nih.gov/pubmed/26789720
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1159/000443684
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