Expression of human factor IX in mice after injection of genetically modified myoblasts.
Hemophilia B is an X chromosome-linked recessive bleeding disorder. To develop a somatic gene therapy for this disease, we have examined whether mouse skeletal myoblasts can serve as efficient vehicles for systemic delivery of recombinant factor IX. When mouse myoblasts (C2C12) transduced with a Mol...
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| Publicado no: | Proc Natl Acad Sci U S A |
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| Principais autores: | , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
National Academy of Sciences
1992
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| Assuntos: | |
| Acesso em linha: | https://ncbi.nlm.nih.govhttps://pmc.ncbi.nlm.nih.gov/articles/PMC48866/ https://ncbi.nlm.nih.govhttps://pubmed.ncbi.nlm.nih.gov/1565626/ https://ncbi.nlm.nih.govhttps://doi.org/10.1073/pnas.89.8.3357 |
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